Studying the Medicine Apitegromab for Babies with Muscle Weakness

About This Study

Spinal muscular atrophy is a disease that makes muscles weak and hard to move. The purpose of this study is to test a new medicine called apitegromab. We want to see if it is safe and helpful for babies under 2 years old who still have trouble moving even though they already got another treatment called survival motor neuron therapy.

What Activities Are a Part of this Study?

Informed Consent Review
Use of Study Treatments or Placebo
After Study Follow-Up Activities
Review of Medical History
Physical Examinations
Phone Calls and/or Emails
Study Visits and Consultations
Surveys/Questionnaires
Laboratory and Imaging Tests
Specimen Sample Collection

Age & Gender

0 - 2 years old
All Genders

Language

This study enrolls English speakers only

Additional Study Information

No compensation provided
Reimbursement offered

Study Locations

Greater Winston-Salem, NC

Study Topics

Bones, Joints, Muscles Children, Infants, Teen Health Genetic Disorders Movement Disorder Neurology Disorders Rare Disease

Study Locations and Contacts

Greater Winston-Salem, NC: Donna Gallimore dgallimo@wakehealth.edu

Study Information
IRB Number: IRB00127698

Helpful Information

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